Bringing you the latest cutting-edge research and commentary in bioscience.

Cell & Gene Therapy Insights

Cell & Gene Therapy Insights

Rare Diseases – Clinical & Commercial Developments

Guest Editors: Dr Sven Kili, Sven Kili Consulting Ltd & Dr Jaap Boelens, Memorial Sloan Kettering Cancer Center The promising early clinical data from gene therapies for rare diseases has seen a resurgence in investment and optimism in the field. This spotlight discusses the current clinical landscape as well as the critical considerations in moving these therapies towards successful commercialization.
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