CELL & GENE THERAPY INSIGHTS

Jul 2018. Vol 4 Issue 7

Jul 2018

FEATURING

Issue Spotlights: Rare Diseases – Clinical & Commercial Developments | Latest Advances in Bioprocessing: Overcoming Bottlenecks
Other articles
Webinar

Spotlight

Latest Advances in Bioprocessing: Overcoming Bottlenecks
Sep 2018
Guest Editor:
Ioannis Papantoniou
Ioannis Papantoniou, ATMP Bioprocess Research Coordinator at KU Leuven
Ioannis Papantoniou
Ioannis Papantoniou
ATMP Bioprocess Research Coordinator at KU Leuven

Expert Insight

Development of purification steps for several AAV serotypes using POROS™ CaptureSelect™ AAVX affinity chromatography

Development of purification steps for several AAV serotypes using POROS™ CaptureSelect™ AAVX affinity chromatography
Magali Toueille,
ESTHER ATTEBI,
L L Dejoint,
Jessica Cartigny,
Céline Rasle,
Stéphanie Potier,
Stéphanie Rundwasser,
Laurence Guianvarc’h,
Matthias Hebben,
Christine Le Bec
1 October 2018
Expert Insight
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Spotlight

Rare Diseases – Clinical & Commercial Developments
Jul 2018
Guest Editor:
Jaap Boelens
Jaap Boelens, Pediatrician-Oncologist, Immunologist at University Medical Centre Utrecht
Jaap Boelens
Jaap Boelens
Pediatrician-Oncologist, Immunologist at University Medical Centre Utrecht

Editorial

Unique Role of Patient Advocacy Groups in Clinical Development of CGTx for Rare Diseases

Unique Role of Patient Advocacy Groups in Clinical Development of CGTx for Rare Diseases
Michelle Berg
16 October 2018
Editorial
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Developing Gene Therapy for CEP290-Associated Retinal Ciliopathies

Developing Gene Therapy for CEP290-Associated Retinal Ciliopathies
Hemant Khanna
2 October 2018
Editorial
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Expert Insight

Advances & challenges in developing gene therapies for rare kidney diseases

Advances & challenges in developing gene therapies for rare kidney diseases
Valeria Padovano,
Michael J Caplan
4 January 2019
Expert Insight
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Gene Therapy for Childhood Cerebral Adrenoleukodystrophy

Gene Therapy for Childhood Cerebral Adrenoleukodystrophy
Christine Duncan
17 October 2018
Expert Insight
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Gene replacement therapy for hemoglobinopathies: clinical benefit & challenges for widespread utilization

Gene replacement therapy for hemoglobinopathies: clinical benefit & challenges for widespread utilization
Marina Cavazzana,
Annarita Miccio,
Isabelle Andre-Schmutz,
Fulvio Mavilio
16 October 2018
Expert Insight
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Interview

SR-TIGET: Continuing to Drive Enabling Technology Development & Clinical Innovation in Rare Diseases

SR-TIGET: Continuing to Drive Enabling Technology Development & Clinical Innovation in Rare Diseases
Alessandro Aiuti
17 October 2018
Interview
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The Critical Role of Patient Advocacy Groups in the Development of Rare Disease Gene Therapies

The Critical Role of Patient Advocacy Groups in the Development of Rare Disease Gene Therapies
Susan Wilson,
Elisabeth Linton
16 October 2018
Interview
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The Future of Gene Therapy for Rare Eye Diseases

The Future of Gene Therapy for Rare Eye Diseases
Aniz Girach
16 October 2018
Interview
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Leukodystrophies: a Patient Advocacy Perspective

Leukodystrophies: a Patient Advocacy Perspective
Maria Kefalas
16 October 2018
Interview
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Advancing the Development of AAV-Based Gene Therapy for Rare Diseases

Advancing the Development of AAV-Based Gene Therapy for Rare Diseases
Suyash Prasad
14 October 2018
Interview
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Other articles

Research Article

A Novel Low Cost High Yield Clinical Scale Cell Separator

A Novel Low Cost High Yield Clinical Scale Cell Separator
PA Liberti,
DW Ritter,
TR Khristov
28 August 2018
Research Article
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Webinars

Making it happen: the road to commercial scale cell therapy manufacturing

Making it happen: the road to commercial scale cell therapy manufacturing
Yonatan Levinson
Yonatan Levinson, Senior Scientist, Allogeneic Bioreactor Platforms, Cell Therapy at Lonza Pharma & Biotech
Thomas Richardson
Thomas Richardson, Scientist II at Lonza Pharma & Biotech
Inbar Friedrich Ben-Nun
Inbar Friedrich Ben-Nun, Senior Manager at Lonza Pharma & Biotech
27 September 2018
Webinar
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