Clinical trial design, supply chain and operations

CELL AND GENE THERAPY INSIGHTS

July 2021

Clinical trial design, supply chain and operations

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Editorial

CRISPR gene editing for sickle cell disease: one disease, differentiated approaches

CRISPR gene editing for sickle cell disease: one disease, differentiated approaches

Lisa A Michaels, MD, Bruce E Eaton, PhD

Innovator Insight

Preparing for pivotal: solving challenges in scale for cell and gene therapy clinical trials

Preparing for pivotal: solving challenges in scale for cell and gene therapy clinical trials

S Viswanathan, R Gaeto, E Goodhue Meyer et al.

Interview

Strengthening the clinical supply chain for individualized therapies

Strengthening the clinical supply chain for individualized therapies

James Andrew Case

Driving clinical progress of gene therapy in cystic fibrosis

Driving clinical progress of gene therapy in cystic fibrosis

Uta Griesenbach

Challenges in the gene therapy of bone marrow failure syndromes

Challenges in the gene therapy of bone marrow failure syndromes

Learning lessons from the long, troubled history of stem cell therapy for future clinical success

Learning lessons from the long, troubled history of stem cell therapy for future clinical success

Addressing issues in clinical development of AAV-driven gene therapy

Addressing issues in clinical development of AAV-driven gene therapy