Translation and Application of Gene Editing

CELL AND GENE THERAPY INSIGHTS

January 2017

Translation and Application of Gene Editing

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Editorial

<em>In vivo</em> genome editing as a therapeutic strategy for treatment of inherited retinal dystrophies: how close are we to realization?

In vivo genome editing as a therapeutic strategy for treatment of inherited retinal dystrophies: how close are we to realization?

8 February 2017

Advances & challenges of using CRISPR-Cas9 gene editing for treating Duchenne muscular dystrophy

Advances & challenges of using CRISPR-Cas9 gene editing for treating Duchenne muscular dystrophy

D L Ouellet, B Duchêne, J Iyombe-Engembe et al.

8 February 2017

Expert Insight

Repurposing CRISPR-Cas systems as DNA-based smart antimicrobials

Repurposing CRISPR-Cas systems as DNA-based smart antimicrobials

Rodolphe Barrangou, David G Ousterout

Current gene editing strategies for the mucopolysaccharidoses

Current gene editing strategies for the mucopolysaccharidoses

M Osborn, D Hyun Yoon, B Hee Lee et al.

8 February 2017

Recent advances in the use of ZFN-mediated gene editing for human gene therapy

Recent advances in the use of ZFN-mediated gene editing for human gene therapy

Srinivasan Chandrasegaran

8 February 2017

Interview

Gene editing of peripheral blood T cells for cancer immunotherapy

Gene editing of peripheral blood T cells for cancer immunotherapy

8 February 2017